Spur Therapeutics Presents Updated Gaucher Gene Therapy Data
Four adults with type 1 Gaucher disease who received a single low dose of avigbagene parvec (FLT201; 4.5e11 vg/kg)...
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Four adults with type 1 Gaucher disease who received a single low dose of avigbagene parvec (FLT201; 4.5e11 vg/kg)...
ARV-102 delivered dose-dependent exposure in plasma and CSF, was well tolerated with no serious adverse events or discontinuations, and...
Topline data: In a prospective, multi-center IDE randomized controlled trial for chronic craniofacial pain, 69% of patients on active...
Quantum BioPharma has received final 90-day oral toxicity and toxicokinetic reports for Lucid-21-302 (Lucid-MS), positioning the program to support...
In a randomized, double-blind Phase 2 study of 77 patients with multiple system atrophy (MSA), ATH434 delivered a clinically...
ANAVEX3-71 met its primary endpoint in a placebo-controlled Phase 2 study in adults with schizophrenia on stable antipsychotic therapy,...
VQ-101 delivered more than 70% activation of lysosomal glucocerebrosidase in GBA-Parkinson’s patients after 28 days of once-daily dosing, exceeding...
ALX Oncology will present updated Phase 2 data from ASPEN-06, indicating that tumor CD47 overexpression may predict response to...
BriaCell will debut preclinical data for Bria-OTS+, an off-the-shelf cancer vaccine platform that aims to combine trained innate immunity...
No new clinical efficacy endpoints were disclosed. Vielight introduced a meditation-specific protocol within its Neuro Pro photobiomodulation device and...